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Clinical trials

Phase 3 Thalassemia trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Thalassemia Phase: Phase 3 Clear all

11 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20021
20031
20041
20052
20121
20161
20211
20222
20251

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed7
Recruiting2
Active, not recruiting1
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Novartis Pharmaceuticals4
Vertex Pharmaceuticals Incorporated3
Lipomed1
Novartis1
Novo Nordisk A/S1
University of Campinas, Brazil1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Thalassemia11
beta-Thalassemia5
Anemia, Sickle Cell4
Iron Overload4
Anemia3
Genetic Diseases, Inborn3
Hematologic Diseases3
Hemoglobinopathies3
Anemia, Diamond-Blackfan2
Hemosiderosis2

Trials

Showing 26 to 11 of 11. Each trial links to its page on Pharma Observatory.

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Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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