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Clinical trials

Thalassemia trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Thalassemia Clear all

218 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20004
20011
20024
20034
20048
20055
20066
20078
200812
200915
20105
20118
201210
20137
201410
20157
20167
201711
201813
20199
20205
20215
202214
20239
202414
20254
20267

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed133
Unknown status23
Terminated19
Recruiting16
Active, not recruiting11
Not yet recruiting7
Withdrawn5
Enrolling by invitation2
Available1
Approved for marketing1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Novartis Pharmaceuticals17
HaEmek Medical Center, Israel11
Carelon Research7
National Heart, Lung, and Blood Institute (NHLBI)7
UCSF Benioff Children's Hospital Oakland6
University of California, San Francisco6
Assiut University5
Novo Nordisk A/S5
Hangzhou Zede Pharma-Tech Co., Ltd.4
St. Jude Children's Research Hospital4

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Thalassemia218
Anemia, Sickle Cell78
beta-Thalassemia42
Hemoglobinopathies36
Iron Overload33
Anemia, Diamond-Blackfan20
Anemia18
Genetic Diseases, Inborn11
Hematologic Diseases11
Myelodysplastic Syndromes11

Trials

Showing 51 to 75 of 218. Each trial links to its page on Pharma Observatory.

118 more trials match. See them on Pharma Observatory

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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