Clinical trials
Phase 1/2 Thalassemia trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
13 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2008 | 2 |
| 2009 | 1 |
| 2011 | 1 |
| 2012 | 2 |
| 2014 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2018 | 1 |
| 2019 | 1 |
| 2022 | 1 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 5 |
| Terminated | 3 |
| Recruiting | 2 |
| Active, not recruiting | 1 |
| Unknown status | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Bellicum Pharmaceuticals | 2 |
| Children's Hospital of Philadelphia | 2 |
| Gamida Cell ltd | 2 |
| Children's Hospital Los Angeles | 1 |
| National Heart, Lung, and Blood Institute (NHLBI) | 1 |
| Nova Laboratories Limited | 1 |
| Talaris Therapeutics Inc. | 1 |
| The Hospital for Sick Children | 1 |
| University of Florida | 1 |
| Weill Medical College of Cornell University | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Thalassemia | 13 |
| Anemia, Sickle Cell | 9 |
| Anemia, Diamond-Blackfan | 4 |
| Anemia | 3 |
| Hemoglobinopathies | 3 |
| Anemia, Aplastic | 2 |
| Bone Marrow Failure Disorders | 2 |
| Cytopenia | 2 |
| Fanconi Anemia | 2 |
| Genetic Diseases, Inborn | 2 |
Trials
Showing 76 to 13 of 13. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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