Clinical trials
Lysosomal Storage Diseases trials in Canada
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
19 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2004 | 2 |
| 2008 | 2 |
| 2010 | 1 |
| 2011 | 4 |
| 2012 | 1 |
| 2014 | 2 |
| 2015 | 1 |
| 2017 | 1 |
| 2019 | 2 |
| 2020 | 2 |
| 2022 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 13 |
| Terminated | 4 |
| Active, not recruiting | 1 |
| Suspended | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| BioMarin Pharmaceutical | 4 |
| Alexion Pharmaceuticals, Inc. | 3 |
| Shire | 3 |
| Gemma Biotherapeutics | 1 |
| Pfizer | 1 |
| Sangamo Therapeutics | 1 |
| Spark Therapeutics, Inc. | 1 |
| Spur Therapeutics | 1 |
| Sumitomo Pharma Switzerland GmbH | 1 |
| Takeda | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal Storage Diseases | 19 |
| Mucopolysaccharidosis IV | 4 |
| Cholesterol Ester Storage Disease | 3 |
| Genetic Diseases, Inborn | 3 |
| Lipid Metabolism Disorders | 3 |
| Metabolic Diseases | 3 |
| Metabolism, Inborn Errors | 3 |
| Mucopolysaccharidosis II | 3 |
| Sudden Infant Death | 3 |
| Wolman Disease | 3 |
Trials
Showing 51 to 19 of 19. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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