Clinical trials
Lysosomal Storage Diseases trials in Germany
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
28 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2004 | 1 |
| 2008 | 1 |
| 2011 | 2 |
| 2012 | 2 |
| 2013 | 1 |
| 2014 | 2 |
| 2015 | 2 |
| 2016 | 1 |
| 2017 | 1 |
| 2018 | 6 |
| 2019 | 3 |
| 2020 | 3 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 12 |
| Terminated | 6 |
| Withdrawn | 5 |
| Recruiting | 2 |
| Unknown status | 2 |
| Active, not recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| BioMarin Pharmaceutical | 5 |
| CENTOGENE GmbH Rostock | 5 |
| Shire | 3 |
| Alexion Pharmaceuticals, Inc. | 2 |
| Spark Therapeutics, Inc. | 2 |
| Spur Therapeutics | 2 |
| ZevraDenmark | 2 |
| Azafaros B.V. | 1 |
| LYSOGENE | 1 |
| Rocket Pharmaceuticals Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal Storage Diseases | 28 |
| Genetic Diseases, Inborn | 6 |
| Metabolic Diseases | 6 |
| Mucopolysaccharidosis IV | 5 |
| Fabry Disease | 4 |
| Lipid Metabolism Disorders | 4 |
| Metabolism, Inborn Errors | 4 |
| Glycogen Storage Disease Type II | 3 |
| Lipidoses | 3 |
| Niemann-Pick Disease, Type C | 3 |
Trials
Showing 76 to 28 of 28. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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