Clinical trials
Lysosomal Storage Diseases trials in the Netherlands
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
15 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2008 | 1 |
| 2010 | 1 |
| 2011 | 3 |
| 2014 | 3 |
| 2018 | 1 |
| 2019 | 2 |
| 2020 | 1 |
| 2022 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 9 |
| Terminated | 2 |
| Active, not recruiting | 1 |
| Recruiting | 1 |
| Suspended | 1 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| BioMarin Pharmaceutical | 3 |
| Shire | 3 |
| Spark Therapeutics, Inc. | 2 |
| Alexion Pharmaceuticals, Inc. | 1 |
| Amicus Therapeutics | 1 |
| Denali Therapeutics Inc. | 1 |
| Gemma Biotherapeutics | 1 |
| JCR Pharmaceuticals Co., Ltd. | 1 |
| LYSOGENE | 1 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal Storage Diseases | 15 |
| Mucopolysaccharidosis III | 4 |
| Mucopolysaccharidosis IV | 3 |
| Genetic Diseases, Inborn | 2 |
| Glycogen Storage Disease Type II | 2 |
| Metabolism, Inborn Errors | 2 |
| Mucopolysaccharidosis II | 2 |
| Brain Diseases, Metabolic, Inborn | 1 |
| Carbohydrate Metabolism, Inborn Errors | 1 |
| Cholesterol Ester Storage Disease | 1 |
Trials
Showing 76 to 15 of 15. Each trial links to its page on Pharma Observatory.
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Recently changed trials
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