Clinical trials
Lysosomal Storage Diseases trials with unknown status
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
10 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2012 | 2 |
| 2013 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2016 | 1 |
| 2018 | 2 |
| 2021 | 1 |
| 2024 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Unknown status | 10 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal and Rare Disorders Research and Treatment Center, Inc. | 2 |
| O & O Alpan LLC | 2 |
| Brigham and Women's Hospital | 1 |
| LYSOGENE | 1 |
| Massachusetts General Hospital | 1 |
| McMaster University | 1 |
| Spital Linth | 1 |
| Wuerzburg University Hospital | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal Storage Diseases | 10 |
| Fabry Disease | 5 |
| Gaucher Disease | 4 |
| Glycogen Storage Disease Type II | 4 |
| Metabolic Diseases | 2 |
| Niemann-Pick Diseases | 2 |
| Cardiomyopathy, Hypertrophic | 1 |
| Cholesterol Ester Storage Disease | 1 |
| Gangliosidoses | 1 |
| Malnutrition | 1 |
Trials
Showing 76 to 10 of 10. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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