Clinical trials
Phase 2/3 Mucopolysaccharidosis II trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
12 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 1 |
| 2004 | 1 |
| 2008 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2018 | 2 |
| 2019 | 1 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 1 |
| 2024 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Active, not recruiting | 5 |
| Completed | 5 |
| Enrolling by invitation | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Shire | 4 |
| Denali Therapeutics Inc. | 2 |
| JCR Pharmaceuticals Co., Ltd. | 2 |
| AO GENERIUM | 1 |
| Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center | 1 |
| REGENXBIO Inc. | 1 |
| Takeda | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis II | 12 |
| Sudden Infant Death | 8 |
| Lysosomal Storage Diseases | 4 |
| Cognition Disorders | 1 |
| Cognitive Dysfunction | 1 |
| Connective Tissue Diseases | 1 |
| Dwarfism | 1 |
| Genetic Diseases, Inborn | 1 |
| Genetic Diseases, X-Linked | 1 |
| Heredodegenerative Disorders, Nervous System | 1 |
Trials
Showing 26 to 12 of 12. Each trial links to its page on Pharma Observatory.
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