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Clinical trials

Phase 2 beta-Thalassemia trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: beta-Thalassemia Phase: Phase 2 Clear all

54 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20001
20011
20031
20042
20051
20061
20082
20091
20101
20112
20124
20131
20144
20173
20181
20194
20203
20214
20224
20232
20242
20263

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed29
Terminated7
Recruiting6
Active, not recruiting4
Unknown status3
Withdrawn3
Not yet recruiting1
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Boston University3
Celgene3
National Institute of Blood and Marrow Transplant (NIBMT), Pakistan3
Novartis Pharmaceuticals3
Shire3
Carelon Research2
National Heart, Lung, and Blood Institute (NHLBI)2
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)2
Vifor (International) Inc.2
Abfero Pharmaceuticals, Inc1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
beta-Thalassemia54
Thalassemia17
Anemia, Sickle Cell14
Iron Overload9
Hematologic Diseases7
Hemoglobinopathies6
Anemia5
Genetic Diseases, Inborn4
Anemia, Diamond-Blackfan3
Anemia, Aplastic2

Trials

Showing 26 to 50 of 54. Each trial links to its page on Pharma Observatory.

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