Skip to content

Clinical trials

Observational alpha 1-Antitrypsin Deficiency trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: alpha 1-Antitrypsin Deficiency Phase: Observational Clear all

45 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20001
20011
20021
20051
20073
20081
20121
20134
20154
20162
20172
20184
20192
20201
20224
20231
20242
20252
20263

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed21
Recruiting9
Unknown status6
Not yet recruiting3
Terminated2
Active, not recruiting2
Enrolling by invitation1
Suspended1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
National Heart, Lung, and Blood Institute (NHLBI)4
University of Florida4
Columbia University3
Medical University of South Carolina3
Alpha-1 Foundation2
Arbor Research Collaborative for Health2
Assiut University2
University Hospital, Bordeaux2
Adverum Biotechnologies, Inc.1
Assistance Publique - Hôpitaux de Paris1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
alpha 1-Antitrypsin Deficiency45
Pulmonary Disease, Chronic Obstructive11
Emphysema8
Genetic Diseases, Inborn5
Cystic Fibrosis4
Lung Diseases3
Alagille Syndrome2
Cholestasis2
Fibrosis2
Inflammation2

Trials

Showing 26 to 45 of 45. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.