Clinical trials
Phase 2 alpha 1-Antitrypsin Deficiency trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
25 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2003 | 1 |
| 2010 | 3 |
| 2012 | 3 |
| 2014 | 2 |
| 2016 | 1 |
| 2017 | 2 |
| 2018 | 2 |
| 2019 | 3 |
| 2020 | 2 |
| 2021 | 2 |
| 2023 | 2 |
| 2024 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 15 |
| Terminated | 5 |
| Withdrawn | 4 |
| Active, not recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Grifols Therapeutics LLC | 4 |
| Arrowhead Pharmaceuticals | 3 |
| Vertex Pharmaceuticals Incorporated | 3 |
| Dicerna Pharmaceuticals, Inc., a Novo Nordisk company | 2 |
| Sanofi | 2 |
| Beacon Therapeutics | 1 |
| Columbia University | 1 |
| Gerard Turino | 1 |
| Kamada, Ltd. | 1 |
| Mereo BioPharma | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| alpha 1-Antitrypsin Deficiency | 25 |
| Emphysema | 7 |
| Pulmonary Disease, Chronic Obstructive | 4 |
| Diabetes Mellitus, Type 1 | 2 |
| Liver Diseases | 2 |
| Lung Diseases | 2 |
| Cystic Fibrosis | 1 |
| Diabetes Mellitus | 1 |
| Liver Cirrhosis | 1 |
Trials
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