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Clinical trials

Terminated alpha 1-Antitrypsin Deficiency trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: alpha 1-Antitrypsin Deficiency Status: Terminated Clear all

18 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20102
20111
20121
20141
20153
20161
20181
20191
20202
20211
20231
20251

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Terminated18

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Baxalta now part of Shire2
Vertex Pharmaceuticals Incorporated2
Alnylam Pharmaceuticals1
Arrowhead Pharmaceuticals1
Columbia University1
Dicerna Pharmaceuticals, Inc., a Novo Nordisk company1
Grifols Therapeutics LLC1
Heidelberg University1
Kamada, Ltd.1
Korro Bio, Inc.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
alpha 1-Antitrypsin Deficiency18
Pulmonary Disease, Chronic Obstructive4
Diabetes Mellitus, Type 12
Emphysema2
Bronchiectasis1
Cough1
Cystic Fibrosis1
Diabetes Mellitus1
Genetic Diseases, Inborn1
Hypertension, Pulmonary1

Trials

Showing 26 to 18 of 18. Each trial links to its page on Pharma Observatory.

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Recently changed trials

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