Clinical trials
Muscular Dystrophy, Duchenne trials in Czechia
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
17 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2010 | 1 |
| 2011 | 1 |
| 2013 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2016 | 1 |
| 2018 | 2 |
| 2019 | 1 |
| 2020 | 4 |
| 2021 | 1 |
| 2024 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 5 |
| Terminated | 5 |
| Active, not recruiting | 2 |
| Recruiting | 2 |
| Unknown status | 2 |
| No longer available | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| PTC Therapeutics | 3 |
| Sarepta Therapeutics, Inc. | 3 |
| GlaxoSmithKline | 2 |
| BioMarin Pharmaceutical | 1 |
| Centre Hospitalier Universitaire de Liege | 1 |
| Italfarmaco | 1 |
| Kyntra Bio | 1 |
| NS Pharma, Inc. | 1 |
| ReveraGen BioPharma, Inc. | 1 |
| Santhera Pharmaceuticals | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Muscular Dystrophy, Duchenne | 17 |
| Muscular Dystrophies | 4 |
| Genetic Diseases, Inborn | 2 |
| Genetic Diseases, X-Linked | 2 |
| Muscular Diseases | 2 |
| Muscular Disorders, Atrophic | 2 |
| Musculoskeletal Diseases | 2 |
| Nervous System Diseases | 2 |
| Neuromuscular Diseases | 2 |
| Charcot-Marie-Tooth Disease | 1 |
Trials
Showing 51 to 17 of 17. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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