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Clinical trials

Phase 1/2 Muscular Dystrophy, Duchenne trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophy, Duchenne Phase: Phase 1/2 Clear all

45 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20021
20052
20071
20092
20101
20111
20136
20143
20154
20163
20172
20183
20192
20201
20211
20222
20231
20244
20253
20262

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed20
Unknown status9
Recruiting6
Active, not recruiting4
Terminated4
Not yet recruiting1
Withdrawn1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Sarepta Therapeutics, Inc.5
BioMarin Pharmaceutical4
Chaitanya Hospital, Pune2
Cooperative International Neuromuscular Research Group2
Craig McDonald, MD2
Entrada Therapeutics, Inc.2
Kevin Flanigan2
Solid Biosciences Inc.2
AO GENERIUM1
Acibadem University1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophy, Duchenne45
Muscular Dystrophies6
Muscular Diseases2
Neuromuscular Diseases2
Cardiomyopathies1
Muscular Dystrophies, Limb-Girdle1
Muscular Dystrophy, Facioscapulohumeral1
Musculoskeletal Diseases1
Nervous System Diseases1
Obesity1

Trials

Showing 26 to 45 of 45. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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