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Clinical trials

Phase 2 Muscular Dystrophy, Duchenne trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophy, Duchenne Phase: Phase 2 Clear all

84 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20011
20021
20052
20061
20083
20091
20105
20113
20121
20133
20145
20152
201611
20173
20187
20194
20204
20212
20225
20233
20247
20255
20264

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed40
Terminated21
Active, not recruiting11
Recruiting4
Enrolling by invitation4
Withdrawn2
Not yet recruiting1
Unknown status1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
PTC Therapeutics8
Sarepta Therapeutics, Inc.7
ReveraGen BioPharma, Inc.5
Capricor Inc.4
Edgewise Therapeutics, Inc.4
NS Pharma, Inc.4
BioMarin Pharmaceutical3
Pfizer3
Santhera Pharmaceuticals3
University of Florida3

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophy, Duchenne84
Muscular Dystrophies15
Neuromuscular Diseases5
Cardiomyopathies2
Tabes Dorsalis2
Aneurysm1
Fatigue1
Fractures, Bone1
Genetic Diseases, Inborn1
Genetic Diseases, X-Linked1

Trials

Showing 26 to 50 of 84. Each trial links to its page on Pharma Observatory.

Recently changed trials

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