Clinical trials
Enrolling by invitation Muscular Dystrophy, Duchenne trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
18 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2013 | 1 |
| 2018 | 1 |
| 2019 | 1 |
| 2023 | 4 |
| 2024 | 2 |
| 2025 | 5 |
| 2026 | 4 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Enrolling by invitation | 18 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lokman Hekim University | 3 |
| Sarepta Therapeutics, Inc. | 3 |
| BioMarin Pharmaceutical | 1 |
| Edgewise Therapeutics, Inc. | 1 |
| Istanbul University | 1 |
| Johns Hopkins University | 1 |
| REGENXBIO Inc. | 1 |
| RTI International | 1 |
| Rigshospitalet, Denmark | 1 |
| Sanko University | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Muscular Dystrophy, Duchenne | 18 |
| Muscular Dystrophies | 3 |
| Angelman Syndrome | 1 |
| Arrhythmogenic Right Ventricular Dysplasia | 1 |
| Brugada Syndrome | 1 |
| Cardiomyopathy, Dilated | 1 |
| Cardiomyopathy, Hypertrophic | 1 |
| Channelopathies | 1 |
| Developmental Disabilities | 1 |
| DiGeorge Syndrome | 1 |
Trials
Showing 26 to 18 of 18. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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