Clinical trials
Genetic Diseases, Inborn trials in China
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
23 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2011 | 1 |
| 2015 | 1 |
| 2016 | 1 |
| 2017 | 3 |
| 2018 | 3 |
| 2019 | 1 |
| 2021 | 3 |
| 2022 | 2 |
| 2023 | 1 |
| 2024 | 4 |
| 2025 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 11 |
| Unknown status | 6 |
| Completed | 5 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Children's Hospital of Fudan University | 3 |
| Genzyme, a Sanofi Company | 2 |
| Sun Yat-Sen Memorial Hospital of Sun Yat-Sen University | 2 |
| Women's Hospital School Of Medicine Zhejiang University | 2 |
| Children's Hospital of Chongqing Medical University | 1 |
| Eye & ENT Hospital of Fudan University | 1 |
| General Hospital of Chinese Armed Police Forces | 1 |
| Guangzhou Institute of Respiratory Disease | 1 |
| Kyntra Bio | 1 |
| PTC Therapeutics | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 23 |
| Genetic Diseases, X-Linked | 4 |
| Congenital Abnormalities | 3 |
| Hematologic Diseases | 3 |
| Blood Coagulation Disorders | 2 |
| Blood Coagulation Disorders, Inherited | 2 |
| Coagulation Protein Disorders | 2 |
| Hemoglobinopathies | 2 |
| Hemophilia A | 2 |
| Hemophilia B | 2 |
Trials
Showing 26 to 23 of 23. Each trial links to its page on Pharma Observatory.
No trials match these filters.
Try a different keyword, or clear a filter.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.