Clinical trials
Genetic Diseases, Inborn trials in India
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
13 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2009 | 2 |
| 2017 | 3 |
| 2018 | 5 |
| 2021 | 1 |
| 2023 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 7 |
| Recruiting | 2 |
| Withdrawn | 2 |
| Active, not recruiting | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| CENTOGENE GmbH Rostock | 2 |
| Genzyme, a Sanofi Company | 2 |
| Quince Therapeutics S.p.A. | 2 |
| Regeneron Pharmaceuticals | 2 |
| Forma Therapeutics, Inc. | 1 |
| Friedreich's Ataxia Research Alliance | 1 |
| JCR Pharmaceuticals Co., Ltd. | 1 |
| PTC Therapeutics | 1 |
| Sumitomo Pharma Switzerland GmbH | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 13 |
| Metabolism, Inborn Errors | 5 |
| Lysosomal Storage Diseases | 4 |
| Metabolic Diseases | 4 |
| Musculoskeletal Diseases | 4 |
| Genetic Diseases, X-Linked | 3 |
| Hematologic Diseases | 3 |
| Arthritis | 2 |
| Blood Coagulation Disorders | 2 |
| Blood Coagulation Disorders, Inherited | 2 |
Trials
Showing 51 to 13 of 13. Each trial links to its page on Pharma Observatory.
No trials match these filters.
Try a different keyword, or clear a filter.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.