Clinical trials
Genetic Diseases, Inborn trials in the Netherlands
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
47 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 1 |
| 2004 | 2 |
| 2006 | 2 |
| 2009 | 3 |
| 2010 | 1 |
| 2011 | 2 |
| 2013 | 1 |
| 2014 | 3 |
| 2015 | 1 |
| 2016 | 3 |
| 2017 | 1 |
| 2018 | 2 |
| 2019 | 6 |
| 2021 | 5 |
| 2022 | 5 |
| 2023 | 1 |
| 2024 | 1 |
| 2025 | 1 |
| 2026 | 5 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 21 |
| Recruiting | 11 |
| Terminated | 5 |
| Unknown status | 5 |
| Active, not recruiting | 4 |
| Enrolling by invitation | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| ModernaTX, Inc. | 5 |
| Pharming Technologies B.V. | 4 |
| Maastricht University Medical Center | 3 |
| Novo Nordisk A/S | 3 |
| Vertex Pharmaceuticals Incorporated | 3 |
| Dicerna Pharmaceuticals, Inc., a Novo Nordisk company | 2 |
| Erasmus Medical Center | 2 |
| Novartis Pharmaceuticals | 2 |
| REGENXBIO Inc. | 2 |
| AIRNA Corporation | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 47 |
| Metabolic Diseases | 9 |
| Metabolism, Inborn Errors | 8 |
| Infant, Newborn, Diseases | 5 |
| Cardiovascular Diseases | 4 |
| Congenital Abnormalities | 4 |
| Lung Diseases | 4 |
| Muscular Diseases | 4 |
| Muscular Disorders, Atrophic | 4 |
| Muscular Dystrophies | 4 |
Trials
Showing 51 to 47 of 47. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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