Skip to content

Clinical trials

Rare Diseases trials in Austria

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Rare Diseases Country / region: Austria Clear all

7 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20222
20233
20241
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Recruiting3
Active, not recruiting1
Completed1
Unknown status1
Withdrawn1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Novartis Pharmaceuticals2
Friedreich's Ataxia Research Alliance1
Johannes Kepler University of Linz1
Medical University of Vienna1
RWTH Aachen University1
Swedish Orphan Biovitrum1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Rare Diseases7
Neurodegenerative Diseases3
Friedreich Ataxia2
Huntington Disease2
Ataxia1
Genetic Diseases, Inborn1
Glomerulonephritis1
Neurologic Manifestations1

Trials

Showing 26 to 7 of 7. Each trial links to its page on Pharma Observatory.

No trials match these filters.

Try a different keyword, or clear a filter.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.