Clinical trials
Rare Diseases trials in Brazil
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
7 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2006 | 1 |
| 2012 | 1 |
| 2015 | 1 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 3 |
| Recruiting | 2 |
| Active, not recruiting | 1 |
| Suspended | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Gemma Biotherapeutics | 2 |
| Amgen | 1 |
| Associazione Angela Serra per la ricerca sul cancro | 1 |
| Children's National Research Institute | 1 |
| Friedreich's Ataxia Research Alliance | 1 |
| Ultragenyx Pharmaceutical Inc | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 7 |
| Lysosomal Storage Diseases | 3 |
| Ataxia | 1 |
| Cystinosis | 1 |
| Friedreich Ataxia | 1 |
| Gangliosidosis, GM1 | 1 |
| Genetic Diseases, Inborn | 1 |
| Leukodystrophy, Globoid Cell | 1 |
| Lymphoma, T-Cell, Peripheral | 1 |
| Metabolic Diseases | 1 |
Trials
Showing 26 to 7 of 7. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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