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Clinical trials

Rare Diseases trials in China

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Rare Diseases Country / region: China Clear all

11 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20182
20211
20221
20241
20253
20262

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Recruiting3
Completed2
Terminated2
Unknown status2
Enrolling by invitation1
Withdrawn1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Peking Union Medical College Hospital2
Associazione Angela Serra per la ricerca sul cancro1
AstraZeneca1
Chu Hongling1
Shandong University1
Swedish Orphan Biovitrum1
The First Affiliated Hospital with Nanjing Medical University1
Third Military Medical University1
Xinhua Hospital, Shanghai Jiao Tong University School of Medicine1
Yongguo Yu1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Rare Diseases11
Disease2
Intellectual Disability2
Abnormalities, Multiple1
Adrenoleukodystrophy1
Blister1
Calciphylaxis1
Developmental Disabilities1
Eosinophilia1
Fanconi Anemia1

Trials

Showing 26 to 11 of 11. Each trial links to its page on Pharma Observatory.

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Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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