Clinical trials
Rare Diseases trials in the Netherlands
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
15 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2010 | 2 |
| 2013 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2018 | 1 |
| 2019 | 1 |
| 2022 | 3 |
| 2023 | 2 |
| 2025 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 5 |
| Completed | 5 |
| Enrolling by invitation | 1 |
| Active, not recruiting | 1 |
| Suspended | 1 |
| Terminated | 1 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Amgen | 3 |
| Novartis Pharmaceuticals | 2 |
| REGENXBIO Inc. | 2 |
| Friedreich's Ataxia Research Alliance | 1 |
| Gemma Biotherapeutics | 1 |
| NightstaRx Ltd, a Biogen Company | 1 |
| Prof. Valérie Mc Lin | 1 |
| Shionogi | 1 |
| Technical University of Madrid | 1 |
| UMC Utrecht | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 15 |
| Metabolic Diseases | 4 |
| Cardiovascular Diseases | 3 |
| Cystinosis | 3 |
| Genetic Diseases, Inborn | 3 |
| Neurodegenerative Diseases | 3 |
| Atherosclerosis | 2 |
| Homozygous Familial Hypercholesterolemia | 2 |
| Huntington Disease | 2 |
| Hyperlipoproteinemia Type II | 2 |
Trials
Showing 51 to 15 of 15. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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