Clinical trials
Phase 2/3 Rare Diseases trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
6 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2006 | 1 |
| 2022 | 1 |
| 2025 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 3 |
| Active, not recruiting | 1 |
| Recruiting | 1 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Hospices Civils de Lyon | 1 |
| Icahn School of Medicine at Mount Sinai | 1 |
| Institut National de la Santé Et de la Recherche Médicale, France | 1 |
| Napo Pharmaceuticals, Inc. | 1 |
| National Center for Research Resources (NCRR) | 1 |
| Rapa Therapeutics LLC | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 6 |
| Amyotrophic Lateral Sclerosis | 1 |
| Arthritis | 1 |
| Arthritis, Juvenile | 1 |
| Communicable Diseases | 1 |
| Congenital, Hereditary, and Neonatal Diseases and Abnormalities | 1 |
| Connective Tissue Diseases | 1 |
| Dystonia | 1 |
| Immune System Diseases | 1 |
| Lupus Erythematosus, Systemic | 1 |
Trials
Showing 26 to 6 of 6. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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