Clinical trials
Active, not recruiting Rare Diseases trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
10 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2017 | 1 |
| 2021 | 2 |
| 2023 | 3 |
| 2024 | 1 |
| 2025 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Active, not recruiting | 10 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| IRCCS Policlinico S. Donato | 2 |
| Fondazione Policlinico Universitario Agostino Gemelli IRCCS | 1 |
| Gemma Biotherapeutics | 1 |
| Hanns Lochmuller | 1 |
| Mario Negri Institute for Pharmacological Research | 1 |
| Meyer Children's Hospital IRCCS | 1 |
| Napo Pharmaceuticals, Inc. | 1 |
| National Cancer Institute (NCI) | 1 |
| Novartis Pharmaceuticals | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 10 |
| Adenocarcinoma, Bronchiolo-Alveolar | 1 |
| Adenocarcinoma, Mucinous | 1 |
| Adrenocortical Carcinoma | 1 |
| Aortic Aneurysm, Thoracic | 1 |
| Basal Cell Carcinoma | 1 |
| Bile Duct Neoplasms | 1 |
| Body Dysmorphic Disorders | 1 |
| Carcinoma, Acinar Cell | 1 |
| Carcinoma, Adenoid Cystic | 1 |
Trials
Showing 26 to 10 of 10. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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