Clinical trials
Terminated Rare Diseases trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
26 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 2 |
| 2001 | 1 |
| 2013 | 1 |
| 2015 | 1 |
| 2016 | 2 |
| 2018 | 2 |
| 2019 | 1 |
| 2021 | 1 |
| 2025 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Terminated | 26 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Center for Research Resources (NCRR) | 3 |
| AstraZeneca | 2 |
| Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | 2 |
| National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | 2 |
| Case Western Reserve University | 1 |
| Emory University | 1 |
| Fairview University Medical Center | 1 |
| Gradalis, Inc. | 1 |
| Hugo W. Moser Research Institute at Kennedy Krieger, Inc. | 1 |
| Institut National de la Santé Et de la Recherche Médicale, France | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Rare Diseases | 26 |
| Genetic Diseases, Inborn | 5 |
| Mental Disorders | 5 |
| Neurologic Manifestations | 5 |
| Metabolism, Inborn Errors | 4 |
| Respiratory Tract Diseases | 3 |
| Adrenoleukodystrophy | 2 |
| Communicable Diseases | 2 |
| Immune System Diseases | 2 |
| Neoplasms | 2 |
Trials
Showing 26 to 26 of 26. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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