Clinical trials
Enrolling by invitation trials in Australia
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
74 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2012 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2016 | 2 |
| 2018 | 2 |
| 2019 | 3 |
| 2020 | 2 |
| 2021 | 6 |
| 2022 | 8 |
| 2023 | 13 |
| 2024 | 12 |
| 2025 | 16 |
| 2026 | 7 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Enrolling by invitation | 74 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Western Sydney Local Health District | 4 |
| QED Therapeutics, a BridgeBio company | 3 |
| BioMarin Pharmaceutical | 2 |
| Endogenex, Inc. | 2 |
| Kite, A Gilead Company | 2 |
| Pharvaris Netherlands B.V. | 2 |
| Sarepta Therapeutics, Inc. | 2 |
| United Therapeutics | 2 |
| Vertex Pharmaceuticals Incorporated | 2 |
| Abbott Medical Devices | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 5 |
| Musculoskeletal Diseases | 5 |
| Bone Diseases | 4 |
| Epilepsy | 4 |
| Angioedemas, Hereditary | 3 |
| Diabetes Mellitus | 3 |
| Dwarfism | 3 |
| Mucopolysaccharidosis IV | 3 |
| Neoplasms | 3 |
| Osteochondrodysplasias | 3 |
Trials
Showing 51 to 74 of 74. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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