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Clinical trials

Completed Phase 2 Homozygous Familial Hypercholesterolemia trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Homozygous Familial Hypercholesterolemia Phase: Phase 2 Status: Completed Clear all

9 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20031
20061
20071
20111
20152
20161
20191
20231

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed9

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Kastle Therapeutics, LLC2
Aegerion Pharmaceuticals, Inc.1
Akeso1
Beijing Suncadia Pharmaceuticals Co., Ltd1
Cerenis Therapeutics, SA1
Gilead Sciences1
Regeneron Pharmaceuticals1
The Medicines Company1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Homozygous Familial Hypercholesterolemia9
Hyperlipoproteinemia Type II3
Congenital Abnormalities1
Dyslipidemias1
Genetic Diseases, Inborn1
Hypercholesterolemia1
Hyperlipidemias1
Hyperlipoproteinemias1
Infant, Newborn, Diseases1
Lipid Metabolism Disorders1

Trials

Showing 1 to 9 of 9. Each trial links to its page on Pharma Observatory.

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