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Clinical trials

Phase 2 Achondroplasia trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Achondroplasia Phase: Phase 2 Clear all

16 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20141
20161
20181
20191
20204
20212
20221
20243
20252

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Active, not recruiting5
Completed5
Recruiting3
Terminated2
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
BioMarin Pharmaceutical5
Ascendis Pharma A/S3
QED Therapeutics, a BridgeBio company3
Pfizer2
Ascendis Pharma Growth Disorders A/S1
Tyra Biosciences, Inc1
Visen Pharmaceuticals (Shanghai) Co., Ltd.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Achondroplasia16
Dwarfism10
Bone Diseases9
Musculoskeletal Diseases7
Mucopolysaccharidosis IV5
Osteochondrodysplasias5
Bone Diseases, Developmental4
Genetic Diseases, Inborn4
Growth Disorders1

Trials

Showing 1 to 16 of 16. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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