Clinical trials
Amino Acid Metabolism, Inborn Errors trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
15 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2006 | 1 |
| 2008 | 1 |
| 2010 | 1 |
| 2014 | 2 |
| 2019 | 1 |
| 2021 | 2 |
| 2024 | 3 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 5 |
| Recruiting | 5 |
| Unknown status | 2 |
| Active, not recruiting | 1 |
| Not yet recruiting | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| ModernaTX, Inc. | 2 |
| National Center for Research Resources (NCRR) | 2 |
| iECURE, Inc. | 2 |
| Andrea Gropman | 1 |
| Brendan Lee | 1 |
| Food and Nutrition Research Institute, Philippines | 1 |
| National Human Genome Research Institute (NHGRI) | 1 |
| PTC Therapeutics | 1 |
| Rigshospitalet, Denmark | 1 |
| University Children's Hospital, Zurich | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Amino Acid Metabolism, Inborn Errors | 15 |
| Metabolism, Inborn Errors | 11 |
| Metabolic Diseases | 7 |
| Urea Cycle Disorders, Inborn | 7 |
| Genetic Diseases, Inborn | 6 |
| Brain Diseases, Metabolic, Inborn | 5 |
| Brain Diseases | 4 |
| Brain Diseases, Metabolic | 4 |
| Central Nervous System Diseases | 3 |
| Nervous System Diseases | 3 |
Trials
Showing 1 to 15 of 15. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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