Clinical trials
Observational Fabry Disease trials in the United Kingdom
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
13 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2008 | 1 |
| 2009 | 1 |
| 2010 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2019 | 1 |
| 2021 | 1 |
| 2022 | 1 |
| 2024 | 3 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 6 |
| Recruiting | 4 |
| Unknown status | 2 |
| Active, not recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Chiesi Farmaceutici S.p.A. | 3 |
| CENTOGENE GmbH Rostock | 2 |
| Manchester University NHS Foundation Trust | 2 |
| Brunel University | 1 |
| Genzyme, a Sanofi Company | 1 |
| Royal Free Hospital NHS Foundation Trust | 1 |
| Sangamo Therapeutics | 1 |
| UK Kidney Association | 1 |
| University College, London | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Fabry Disease | 13 |
| Angiokeratoma | 1 |
| Atypical Hemolytic Uremic Syndrome | 1 |
| Bartter Syndrome | 1 |
| Calciphylaxis | 1 |
| Cardiomyopathies | 1 |
| Cystinosis | 1 |
| Cystinuria | 1 |
| Dent Disease | 1 |
| Denys-Drash Syndrome | 1 |
Trials
Showing 1 to 13 of 13. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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