Clinical trials
Fabry Disease trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
93 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2001 | 4 |
| 2002 | 4 |
| 2003 | 4 |
| 2004 | 4 |
| 2005 | 1 |
| 2006 | 4 |
| 2007 | 2 |
| 2008 | 2 |
| 2009 | 2 |
| 2010 | 5 |
| 2011 | 6 |
| 2012 | 4 |
| 2013 | 2 |
| 2014 | 4 |
| 2015 | 2 |
| 2016 | 4 |
| 2017 | 1 |
| 2018 | 7 |
| 2019 | 3 |
| 2020 | 4 |
| 2021 | 2 |
| 2022 | 4 |
| 2023 | 5 |
| 2024 | 2 |
| 2025 | 3 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 56 |
| Recruiting | 10 |
| Terminated | 9 |
| Active, not recruiting | 6 |
| Unknown status | 6 |
| Withdrawn | 3 |
| No longer available | 1 |
| Enrolling by invitation | 1 |
| Approved for marketing | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Amicus Therapeutics | 18 |
| Genzyme, a Sanofi Company | 13 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 11 |
| Chiesi Farmaceutici S.p.A. | 7 |
| Shire | 6 |
| Protalix | 4 |
| Baylor Research Institute | 3 |
| Massachusetts General Hospital | 3 |
| O & O Alpan LLC | 3 |
| Sanofi | 3 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Fabry Disease | 93 |
| Lysosomal Storage Diseases | 10 |
| Stroke | 9 |
| Proteinuria | 6 |
| Gaucher Disease | 4 |
| Glycogen Storage Disease Type II | 3 |
| Hypohidrosis | 3 |
| Kidney Failure, Chronic | 3 |
| Niemann-Pick Diseases | 3 |
| Angiokeratoma | 2 |
Trials
Showing 1 to 25 of 93. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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