Clinical trials
Observational Fabry Disease trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
34 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2001 | 3 |
| 2002 | 1 |
| 2003 | 1 |
| 2005 | 1 |
| 2007 | 1 |
| 2009 | 1 |
| 2010 | 4 |
| 2012 | 1 |
| 2013 | 1 |
| 2014 | 2 |
| 2016 | 1 |
| 2018 | 1 |
| 2020 | 2 |
| 2021 | 2 |
| 2022 | 1 |
| 2023 | 4 |
| 2024 | 1 |
| 2025 | 2 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 16 |
| Recruiting | 7 |
| Unknown status | 6 |
| Terminated | 2 |
| Enrolling by invitation | 1 |
| Active, not recruiting | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Institute of Neurological Disorders and Stroke (NINDS) | 6 |
| Amicus Therapeutics | 4 |
| Chiesi Farmaceutici S.p.A. | 3 |
| O & O Alpan LLC | 3 |
| Baylor Research Institute | 2 |
| Lysosomal and Rare Disorders Research and Treatment Center, Inc. | 2 |
| University of Alabama at Birmingham | 2 |
| Albert Einstein College of Medicine | 1 |
| Boston Children's Hospital | 1 |
| Cedars-Sinai Medical Center | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Fabry Disease | 34 |
| Gaucher Disease | 4 |
| Glycogen Storage Disease Type II | 3 |
| Lysosomal Storage Diseases | 3 |
| Niemann-Pick Diseases | 3 |
| Proteinuria | 3 |
| Stroke | 3 |
| Angiokeratoma | 2 |
| Kidney Failure, Chronic | 2 |
| Rare Diseases | 2 |
Trials
Showing 1 to 25 of 34. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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