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Clinical trials

Phase 3 Fabry Disease trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Fabry Disease Phase: Phase 3 Country / region: United States Clear all

20 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20082
20091
20101
20112
20151
20161
20171
20185
20191
20223
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed14
Active, not recruiting4
Recruiting1
Terminated1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Amicus Therapeutics8
Chiesi Farmaceutici S.p.A.2
Genzyme, a Sanofi Company2
Idorsia Pharmaceuticals Ltd.2
Protalix2
Sanofi2
Shire2

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Fabry Disease20
Proteinuria3
Kidney Diseases1
Kidney Failure, Chronic1
Lysosomal Storage Diseases1
Renal Insufficiency1

Trials

Showing 1 to 20 of 20. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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