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Clinical trials

Recruiting Fabry Disease trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Fabry Disease Status: Recruiting Country / region: United States Clear all

10 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20011
20101
20231
20242
20253
20262

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Recruiting10

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Amicus Therapeutics3
Chiesi Farmaceutici S.p.A.3
Genzyme, a Sanofi Company1
Montefiore Medical Center1
UniQure Biopharma B.V.1
University of Minnesota1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Fabry Disease10
Amyloid Neuropathies, Familial1
Angiokeratoma1
Arrhythmogenic Right Ventricular Dysplasia1
Cardiomyopathies1
Cardiomyopathy, Hypertrophic1
Heart Failure1
Pregnancy Complications1
Sarcoidosis1

Trials

Showing 1 to 10 of 10. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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