Clinical trials
Completed Observational Fabry Disease trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
50 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2001 | 2 |
| 2002 | 1 |
| 2003 | 1 |
| 2004 | 2 |
| 2005 | 1 |
| 2007 | 2 |
| 2008 | 2 |
| 2009 | 2 |
| 2010 | 5 |
| 2011 | 2 |
| 2012 | 2 |
| 2014 | 4 |
| 2015 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2018 | 2 |
| 2019 | 1 |
| 2020 | 3 |
| 2021 | 3 |
| 2022 | 3 |
| 2023 | 4 |
| 2024 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 50 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Institute of Neurological Disorders and Stroke (NINDS) | 6 |
| CENTOGENE GmbH Rostock | 4 |
| Shire | 3 |
| Amicus Therapeutics | 2 |
| Amicus Therapeutics France SAS | 2 |
| Baylor Research Institute | 2 |
| Ulla Feldt-Rasmussen | 2 |
| University of Alabama at Birmingham | 2 |
| Assistance Publique - Hôpitaux de Paris | 1 |
| Brunel University | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Fabry Disease | 50 |
| Stroke | 7 |
| Proteinuria | 3 |
| Cardiomyopathies | 2 |
| Heart Diseases | 2 |
| Hypertrophy, Left Ventricular | 2 |
| Renal Insufficiency, Chronic | 2 |
| Alopecia | 1 |
| Angiokeratoma | 1 |
| CADASIL | 1 |
Trials
Showing 1 to 25 of 50. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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