Skip to content

Clinical trials

Active, not recruiting Fabry Disease trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Fabry Disease Status: Active, not recruiting Clear all

10 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20181
20191
20201
20211
20224
20232

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Active, not recruiting10

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Sanofi3
4D Molecular Therapeutics1
Amicus Therapeutics1
Chinese University of Hong Kong1
Idorsia Pharmaceuticals Ltd.1
Sangamo Therapeutics1
University Hospital Birmingham NHS Foundation Trust1
Universität Münster1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Fabry Disease10
Brain Diseases, Metabolic1
Cardiovascular Diseases1
Central Nervous System Diseases1
Cerebral Small Vessel Diseases1
Cerebrovascular Disorders1
Genetic Diseases, Inborn1
Kidney Diseases1
Kidney Failure, Chronic1
Lipid Metabolism Disorders1

Trials

Showing 1 to 10 of 10. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.