Clinical trials
Observational Charcot-Marie-Tooth Disease trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
21 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2010 | 3 |
| 2011 | 1 |
| 2012 | 1 |
| 2013 | 2 |
| 2014 | 2 |
| 2015 | 1 |
| 2016 | 3 |
| 2017 | 1 |
| 2018 | 1 |
| 2019 | 1 |
| 2020 | 1 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 1 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 9 |
| Recruiting | 7 |
| Terminated | 3 |
| Unknown status | 2 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| University of Iowa | 4 |
| Children's Hospital of Philadelphia | 2 |
| Nemours Children's Clinic | 2 |
| University of South Florida | 2 |
| Foundation Fighting Blindness | 1 |
| Hereditary Neuropathy Foundation | 1 |
| Michael Shy | 1 |
| NMD Pharma A/S | 1 |
| National Human Genome Research Institute (NHGRI) | 1 |
| Neurogene Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Charcot-Marie-Tooth Disease | 21 |
| Refsum Disease | 4 |
| Hereditary Sensory and Motor Neuropathy | 3 |
| Adrenoleukodystrophy | 2 |
| Alexander Disease | 2 |
| Amyotrophic Lateral Sclerosis | 2 |
| Attention Deficit Disorder with Hyperactivity | 2 |
| CADASIL | 2 |
| Canavan Disease | 2 |
| Cockayne Syndrome | 2 |
Trials
Showing 1 to 21 of 21. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
Go deeper on Pharma Observatory
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