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Clinical trials

Observational Dwarfism trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Dwarfism Phase: Observational Country / region: United States Clear all

18 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20011
20053
20061
20081
20122
20141
20181
20193
20211
20221
20241

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed11
Recruiting3
Terminated3
Unknown status1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)3
Nemours Children's Clinic3
Massachusetts General Hospital2
National Human Genome Research Institute (NHGRI)2
QED Therapeutics, a BridgeBio company2
Ascendis Pharma A/S1
BioMarin Pharmaceutical1
Ipsen1
Tripler Army Medical Center1
University of Louisville1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Dwarfism18
Achondroplasia5
Mucopolysaccharidosis IV5
Dwarfism, Pituitary3
Bone Diseases2
Genetic Diseases, Inborn2
Insulin Resistance2
Musculoskeletal Diseases2
Osteochondrodysplasias2
Bone Diseases, Developmental1

Trials

Showing 1 to 18 of 18. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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