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Clinical trials

Completed Dwarfism trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Dwarfism Status: Completed Country / region: United States Clear all

31 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20012
20042
20054
20081
20091
20102
20122
20141
20151
20161
20183
20193
20203
20231

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed31

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
BioMarin Pharmaceutical4
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)4
Nemours Children's Clinic4
QED Therapeutics, a BridgeBio company3
Ascendis Pharma A/S2
Children's Hospital Medical Center, Cincinnati2
National Human Genome Research Institute (NHGRI)2
Arkansas Children's Hospital Research Institute1
DNage B.V.1
Nationwide Children's Hospital1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Dwarfism31
Achondroplasia11
Dwarfism, Pituitary8
Bone Diseases6
Genetic Diseases, Inborn6
Bone Diseases, Developmental5
Musculoskeletal Diseases5
Osteochondrodysplasias5
Mucopolysaccharidosis IV4
Failure to Thrive2

Trials

Showing 1 to 25 of 31. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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