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Clinical trials

Observational Dwarfism trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Dwarfism Phase: Observational Clear all

31 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20011
20054
20061
20081
20091
20122
20141
20151
20161
20181
20193
20201
20214
20223
20232
20241
20251

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed19
Recruiting4
Terminated3
Unknown status3
Active, not recruiting1
Not yet recruiting1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)3
Istituto Auxologico Italiano3
Nemours Children's Clinic3
Cairo University2
Massachusetts General Hospital2
National Human Genome Research Institute (NHGRI)2
QED Therapeutics, a BridgeBio company2
Ascendis Pharma A/S1
BioMarin Pharmaceutical1
HaEmek Medical Center, Israel1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Dwarfism31
Mucopolysaccharidosis IV6
Achondroplasia5
Dwarfism, Pituitary5
Bone Diseases3
Genetic Diseases, Inborn2
Growth Disorders2
Insulin Resistance2
Musculoskeletal Diseases2
Osteochondrodysplasias2

Trials

Showing 1 to 25 of 31. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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