Skip to content

Clinical trials

Completed Observational Dwarfism trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Dwarfism Phase: Observational Status: Completed Clear all

19 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20011
20052
20081
20091
20122
20151
20181
20193
20201
20212
20232

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed19

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Istituto Auxologico Italiano2
National Human Genome Research Institute (NHGRI)2
Nemours Children's Clinic2
Ascendis Pharma A/S1
BioMarin Pharmaceutical1
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)1
HaEmek Medical Center, Israel1
Hospices Civils de Lyon1
Manchester University NHS Foundation Trust1
QED Therapeutics, a BridgeBio company1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Dwarfism19
Achondroplasia5
Dwarfism, Pituitary4
Mucopolysaccharidosis IV2
Adrenal Hyperplasia, Congenital1
Bone Diseases1
Bone Diseases, Developmental1
Failure to Thrive1
Genetic Diseases, Inborn1
Growth Disorders1

Trials

Showing 1 to 19 of 19. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.