Clinical trials
Gaucher Disease trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
173 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2002 | 1 |
| 2004 | 1 |
| 2005 | 2 |
| 2006 | 4 |
| 2007 | 5 |
| 2008 | 6 |
| 2009 | 6 |
| 2010 | 7 |
| 2011 | 11 |
| 2012 | 6 |
| 2013 | 5 |
| 2014 | 7 |
| 2015 | 10 |
| 2016 | 4 |
| 2017 | 5 |
| 2018 | 9 |
| 2019 | 10 |
| 2020 | 7 |
| 2021 | 9 |
| 2022 | 10 |
| 2023 | 12 |
| 2024 | 11 |
| 2025 | 1 |
| 2026 | 7 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 91 |
| Recruiting | 23 |
| Unknown status | 22 |
| Active, not recruiting | 10 |
| Withdrawn | 7 |
| Not yet recruiting | 7 |
| Terminated | 6 |
| Enrolling by invitation | 3 |
| No longer available | 1 |
| Suspended | 1 |
| Available | 1 |
| Approved for marketing | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Shire | 14 |
| Genzyme, a Sanofi Company | 12 |
| Sanofi | 11 |
| Pfizer | 8 |
| Shaare Zedek Medical Center | 7 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 6 |
| Takeda | 6 |
| University of Minnesota | 6 |
| Amicus Therapeutics | 5 |
| ISU Abxis Co., Ltd. | 5 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Gaucher Disease | 173 |
| Lysosomal Storage Diseases | 13 |
| Niemann-Pick Diseases | 10 |
| Metabolism, Inborn Errors | 9 |
| Parkinson Disease | 9 |
| Fabry Disease | 7 |
| Leukodystrophy, Metachromatic | 7 |
| Rare Diseases | 7 |
| Wolman Disease | 7 |
| Adrenoleukodystrophy | 6 |
Trials
Showing 1 to 25 of 173. Each trial links to its page on Pharma Observatory.
73 more trials match. See them on Pharma Observatory
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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