Clinical trials
Phase 1 Gaucher Disease trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
14 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2009 | 1 |
| 2011 | 1 |
| 2013 | 1 |
| 2014 | 1 |
| 2015 | 3 |
| 2018 | 1 |
| 2019 | 1 |
| 2021 | 1 |
| 2022 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 11 |
| Recruiting | 2 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Sanofi | 3 |
| Genzyme, a Sanofi Company | 2 |
| Amicus Therapeutics | 1 |
| National Center for Research Resources (NCRR) | 1 |
| National Institute of Mental Health (NIMH) | 1 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 1 |
| New York Medical College | 1 |
| Spur Therapeutics | 1 |
| UNC Lineberger Comprehensive Cancer Center | 1 |
| University of California, San Francisco | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Gaucher Disease | 14 |
| Metabolism, Inborn Errors | 3 |
| Mucopolysaccharidosis VI | 2 |
| Wolman Disease | 2 |
| Adrenoleukodystrophy | 1 |
| Anemia, Aplastic | 1 |
| Anemia, Diamond-Blackfan | 1 |
| Fucosidosis | 1 |
| Genetic Diseases, Inborn | 1 |
| Leukemia, Myeloid, Acute | 1 |
Trials
Showing 1 to 14 of 14. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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