Clinical trials
Completed Gaucher Disease trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
47 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2002 | 1 |
| 2005 | 1 |
| 2006 | 3 |
| 2007 | 4 |
| 2008 | 5 |
| 2009 | 3 |
| 2010 | 2 |
| 2011 | 4 |
| 2013 | 1 |
| 2014 | 1 |
| 2015 | 4 |
| 2016 | 2 |
| 2018 | 1 |
| 2019 | 2 |
| 2021 | 2 |
| 2022 | 1 |
| 2024 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 47 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genzyme, a Sanofi Company | 8 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 6 |
| Amicus Therapeutics | 4 |
| Sanofi | 4 |
| Shire | 4 |
| Pfizer | 3 |
| University of Minnesota | 3 |
| National Human Genome Research Institute (NHGRI) | 2 |
| Takeda | 2 |
| Children's Hospital Medical Center, Cincinnati | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Gaucher Disease | 47 |
| Metabolism, Inborn Errors | 5 |
| Parkinson Disease | 4 |
| Lysosomal Storage Diseases | 3 |
| Sphingolipidoses | 3 |
| Adrenoleukodystrophy | 2 |
| Fucosidosis | 2 |
| Gangliosidosis, GM1 | 2 |
| Genetic Diseases, Inborn | 2 |
| Leukodystrophy, Globoid Cell | 2 |
Trials
Showing 1 to 25 of 47. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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