Clinical trials
Completed Observational Gaucher Disease trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
26 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2005 | 1 |
| 2006 | 2 |
| 2007 | 1 |
| 2010 | 2 |
| 2011 | 5 |
| 2014 | 1 |
| 2015 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2018 | 1 |
| 2019 | 2 |
| 2021 | 3 |
| 2022 | 2 |
| 2023 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 26 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Institute of Neurological Disorders and Stroke (NINDS) | 3 |
| Takeda | 3 |
| National Human Genome Research Institute (NHGRI) | 2 |
| Sanofi | 2 |
| Shire | 2 |
| Amicus Therapeutics | 1 |
| CEN Biotech | 1 |
| CENTOGENE GmbH Rostock | 1 |
| Centre Hospitalier Universitaire de Liege | 1 |
| Fundación Española de Hematología y Hemoterapía | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Gaucher Disease | 26 |
| Lysosomal Storage Diseases | 3 |
| Parkinson Disease | 3 |
| Splenomegaly | 3 |
| Niemann-Pick Diseases | 2 |
| Sphingolipidoses | 2 |
| Adrenal Hyperplasia, Congenital | 1 |
| Adrenoleukodystrophy | 1 |
| Andersen Syndrome | 1 |
| Anemia, Diamond-Blackfan | 1 |
Trials
Showing 1 to 25 of 26. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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