Clinical trials
Observational Gaucher Disease trials with unknown status
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
13 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2010 | 1 |
| 2011 | 1 |
| 2013 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2016 | 1 |
| 2018 | 2 |
| 2019 | 1 |
| 2022 | 1 |
| 2023 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Unknown status | 13 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal and Rare Disorders Research and Treatment Center, Inc. | 5 |
| O & O Alpan LLC | 2 |
| Assiut University | 1 |
| Fairview University Medical Center | 1 |
| New York Stem Cell Foundation Research Institute | 1 |
| Rabin Medical Center | 1 |
| Shaare Zedek Medical Center | 1 |
| Yasmeen Abd Elbaset Hamzaa | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Gaucher Disease | 13 |
| Fabry Disease | 3 |
| Glycogen Storage Disease Type II | 3 |
| Lysosomal Storage Diseases | 3 |
| Niemann-Pick Diseases | 3 |
| Parkinson Disease | 2 |
| Adrenoleukodystrophy | 1 |
| Blood Platelet Disorders | 1 |
| Bone Diseases | 1 |
| Fucosidosis | 1 |
Trials
Showing 1 to 13 of 13. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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