Clinical trials
Glycogen Storage Disease Type II trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
82 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2003 | 4 |
| 2004 | 3 |
| 2005 | 3 |
| 2007 | 5 |
| 2008 | 4 |
| 2009 | 2 |
| 2010 | 2 |
| 2011 | 4 |
| 2012 | 6 |
| 2013 | 6 |
| 2014 | 3 |
| 2015 | 6 |
| 2016 | 5 |
| 2017 | 5 |
| 2018 | 3 |
| 2019 | 3 |
| 2020 | 3 |
| 2021 | 2 |
| 2022 | 2 |
| 2023 | 1 |
| 2024 | 3 |
| 2025 | 1 |
| 2026 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 49 |
| Recruiting | 11 |
| Active, not recruiting | 8 |
| Terminated | 7 |
| Unknown status | 4 |
| Withdrawn | 2 |
| Approved for marketing | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genzyme, a Sanofi Company | 25 |
| Duke University | 12 |
| Amicus Therapeutics | 8 |
| University of Florida | 7 |
| O & O Alpan LLC | 3 |
| Sanofi | 3 |
| AskBio Inc | 2 |
| Astellas Gene Therapies | 2 |
| BioMarin Pharmaceutical | 2 |
| Spark Therapeutics, Inc. | 2 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Glycogen Storage Disease Type II | 82 |
| Lysosomal Storage Diseases | 7 |
| Glycogen Storage Disease | 5 |
| Gaucher Disease | 4 |
| Fabry Disease | 3 |
| Macular Degeneration | 3 |
| Amyotrophic Lateral Sclerosis | 2 |
| Anemia, Sickle Cell | 2 |
| Cystic Fibrosis | 2 |
| Muscular Atrophy, Spinal | 2 |
Trials
Showing 1 to 25 of 82. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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