Clinical trials
Phase 1/2 Glycogen Storage Disease Type II trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
12 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 1 |
| 2007 | 1 |
| 2010 | 1 |
| 2011 | 1 |
| 2013 | 2 |
| 2014 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2020 | 2 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 8 |
| Active, not recruiting | 2 |
| Recruiting | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Amicus Therapeutics | 1 |
| AskBio Inc | 1 |
| Astellas Gene Therapies | 1 |
| BioMarin Pharmaceutical | 1 |
| Duke University | 1 |
| Dwight Koeberl, M.D., Ph.D. | 1 |
| Genzyme, a Sanofi Company | 1 |
| Retina Research Foundation | 1 |
| Southern California Desert Retina Consultants, MC | 1 |
| Spark Therapeutics, Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Glycogen Storage Disease Type II | 12 |
| Glycogen Storage Disease | 3 |
| Lysosomal Storage Diseases | 2 |
| Macular Degeneration | 2 |
| Fibrosis | 1 |
| Neuromuscular Diseases | 1 |
| Scotoma | 1 |
| Wet Macular Degeneration | 1 |
Trials
Showing 1 to 12 of 12. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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