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Clinical trials

Phase 3 Hematologic Diseases trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Hematologic Diseases Phase: Phase 3 Country / region: United States Clear all

52 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20001
20032
20061
20104
20111
20122
20132
20143
20151
20172
20183
20192
20203
20219
20229
20241
20253
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed22
Active, not recruiting13
Terminated8
Recruiting7
Enrolling by invitation1
Withdrawn1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Pfizer6
Loxo Oncology, Inc.5
Vertex Pharmaceuticals Incorporated4
BioMarin Pharmaceutical3
Ellodi Pharmaceuticals, LP3
National Heart, Lung, and Blood Institute (NHLBI)3
Agios Pharmaceuticals, Inc.2
CTI BioPharma2
Genzyme, a Sanofi Company2
Novartis Pharmaceuticals2

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Hematologic Diseases52
Hemorrhagic Disorders12
Anemia, Sickle Cell11
Genetic Diseases, Inborn10
Anemia8
Blood Coagulation Disorders8
Hemophilia A8
Bone Marrow Diseases7
Coagulation Protein Disorders7
Blood Coagulation Disorders, Inherited6

Trials

Showing 1 to 25 of 52. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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